Research ArticleHEALTH AND MEDICINE

CRISPR-Cas9–mediated therapeutic editing of Rpe65 ameliorates the disease phenotypes in a mouse model of Leber congenital amaurosis

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Science Advances  30 Oct 2019:
Vol. 5, no. 10, eaax1210
DOI: 10.1126/sciadv.aax1210
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