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Research ArticleHEALTH AND MEDICINE
Brain-targeted enzyme-loaded nanoparticles: A breach through the blood-brain barrier for enzyme replacement therapy in Krabbe disease
- View ORCID ProfileAmbra Del Grosso1,*,
- View ORCID ProfileMarianna Galliani1,2,*,
- Lucia Angella1,
- View ORCID ProfileMelissa Santi2,
- View ORCID ProfileIlaria Tonazzini1,
- View ORCID ProfileGabriele Parlanti1,
- View ORCID ProfileGiovanni Signore1,3,† and
- View ORCID ProfileMarco Cecchini1,†
- 1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
- 2Center for Nanotechnology Innovation@NEST, Piazza San Silvestro 12, 56127 Pisa, Italy.
- 3Fondazione Pisana per la Scienza ONLUS, 56017 Pisa, Italy.
- ↵†Corresponding author. Email: marco.cecchini{at}nano.cnr.it (M.C.); g.signore{at}fpscience.it (G.S.)
↵* These authors contributed equally to this work.
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Science Advances 20 Nov 2019:
Vol. 5, no. 11, eaax7462
DOI: 10.1126/sciadv.aax7462
Vol. 5, no. 11, eaax7462
DOI: 10.1126/sciadv.aax7462
Ambra Del Grosso
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
Marianna Galliani
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
2Center for Nanotechnology Innovation@NEST, Piazza San Silvestro 12, 56127 Pisa, Italy.
Lucia Angella
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
Melissa Santi
2Center for Nanotechnology Innovation@NEST, Piazza San Silvestro 12, 56127 Pisa, Italy.
Ilaria Tonazzini
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
Gabriele Parlanti
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
Giovanni Signore
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
3Fondazione Pisana per la Scienza ONLUS, 56017 Pisa, Italy.
Marco Cecchini
1NEST, Istituto Nanoscienze-CNR and Scuola Normale Superiore, Piazza San Silvestro 12, 56127 Pisa, Italy.
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